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A Medical Breakthrough With Gene Therapy: An Interview With Author Maria Kefalas
Getting A Diagnosis For Cal: An Interview With Author Maria Kefalas
MLD Gene Therapy Gains Approval in the EU
Gene Editing
2021 Year in Review | Cure MLD
Gene Therapy for Cerebral Adrenoleukodystrophy
Stem Cell Gene Therapy Shows Promise for Metachromatic Leukodystrophy
ICER CTAF Public Meeting on Metachromatic Leukodystrophy: Public Comment
ACHDNC Meeting January 2024 - Day 1
